FDA Update for Week of April 22, 2024: Second Gene Therapy for Hemophilia B
FDA Approves Pfizer’s Gene Therapy for Beqvez for Hemophilia B The FDA has approved Pfizer’s one-time gene therapy Beqvez (fidanacogene elaparvovec-dzkt) to treat adults with moderate-to-severe hemophilia B. It is indicated for those who currently use …